In this paper, Lina Montoya and Maya Petersen present a robust and efficient approach using targeted maximum likelihood estimation (TMLE) for estimating and contrasting expected outcomes under the dynamic regimes embedded in a SMART, together with generating simultaneous confidence intervals for the resulting estimates.
Balzer LB, Havlir DV, Kamya MR, Chamie G, Charlebois ED, Clark TD, Koss CA, Kwarisiima D, Ayieko J, Sang N, Kabami J, Atukunda M, Jain V, Camlin CS, Cohen CR, Bukusi EA, van der Laan M, Petersen ML.
Hubbard, Alan; Munoz, Ivan Diaz; Decker, Anna; Holcomb, John B.; Schreiber, Martin A.; Bulger, Eileen M.; Brasel, Karen J.; Fox, Erin E.; del Junco, Deborah J.; Wade, Charles E.; others